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MS
CBS AR unreviewed

Homocystinuria (CBS deficiency)

Methionine cycle / transsulfuration Cystathionine beta-synthase

Enzyme or protein defect

Cystathionine beta-synthase

Accumulates or becomes deficient

Homocysteine, methionine

Key features

Marfanoid habitus, DOWNWARD lens dislocation, thrombosis, intellectual disability, osteoporosis

Management

B6 (pyridoxine) trial, betaine, Met restriction, cysteine supplement

Not clinical guidance. Written from standard clinical biochemistry, not from the uploaded documents, and marked unreviewed. Teaching-level reference for study and database seeding only. It must not be used to manage a patient.

Recent literature

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